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JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatment | Gene Therapy
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Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
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IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Frontiers | New Insights Into Pathophysiology of β-Thalassemia
Sirolimus for Treatment of β-Thalassemia: From Pre-Clinical Studies to the Design of Clinical Trials
An urgent need for improving thalassemia care due to the wide gap in current real-life practice and clinical practice guidelines | Scientific Reports
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
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Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Gene Therapy For Beta-Thalassemia: Updated Perspectives | TACG
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Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Current and future alternative therapies for beta-thalassemia major - ScienceDirect
Tricuspid-valve regurgitant jet velocity as a risk factor for death in β- thalassemia | Haematologica
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
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Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon
Thalassaemia - The Lancet
